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@ARTICLE{LeRhun:306583,
author = {E. Le Rhun and D. Sain and S. C. Erridge and D. A. Reardon
and G. Minniti and P. Roth and W. Wick$^*$ and B. Nabors and
J. Sampson and W. Mason and T. Cloughesy and J. C.
Reijneveld and R. Stupp and M. Preusser and T. Gorlia and M.
Weller},
title = {{P}roton {P}ump {I}nhibitor {U}se and {S}urvival in
{P}atients {W}ith {N}ewly {D}iagnosed {G}lioblastoma.},
journal = {JAMA network open},
volume = {8},
number = {11},
issn = {2574-3805},
address = {Chicago, Ill.},
publisher = {American Medical Association},
reportid = {DKFZ-2025-02624},
pages = {e2545578 -},
year = {2025},
abstract = {Proton pump inhibitors (PPI) are often prescribed to
prevent steroid-induced gastritis and peptic ulcer disease
in patients with glioblastoma. Yet, these drugs may enhance
the activity of aldehyde dehydrogenase 1 A1 (ALDH1A1), which
has been linked to protection from oxidative stress,
radiotherapy, and chemotherapy.To explore the associations
of the use of potent ALDH1A1-activating PPIs (PA-PPIs) and
other antacid drugs with outcomes in patients with newly
diagnosed glioblastoma.This meta-analysis was a secondary
analysis of individual prospectively captured patient data
using a dataset of 5 randomized clinical trials conducted
between 2008 and 2020. Participants included patients with a
new diagnosis of glioblastoma. Data analysis was completed
in November 2024.We assessed drug use at baseline and
defined 3 landmarks: start of temozolomide maintenance
cycles 1 (landmark 1) and 4 (landmark 2), and end of cycle 6
(landmark 3).The primary outcome measures were
progression-free survival (PFS) and overall survival (OS)
from baseline and from the start of each corresponding
landmark time.The study population included 2981 patients
(1858 $[62.3\%]$ male; median [range] age, 58 [18-85]
years). On univariate analysis, patients treated with PA-PPI
had worse PFS and OS at all 4 time points. The multivariate
analysis accounting for age, sex, performance status,
steroid use, extent of resection, and MGMT status confirmed
a difference for PFS at landmarks 1 (hazard ratio [HR], 1.14
$[95\%$ CI, 1.01-1.28]), 2 (HR, 1.26 $[95\%$ CI,
1.09-1.44]), and 3 (HR, 1.31 $[95\%$ CI, 1.10-1.56]), and
for OS at landmarks 1 (HR, 1.34 $[95\%$ CI, 1.08-1.66]) and
2 (HR, 1.14 $[95\%$ CI, 1.01-1.29]). No such association was
seen for the use of other antacid drugs. The negative
association of PA-PPI use with PFS and OS was observed
independently of MGMT promoter methylation and steroid
use.In this meta-analysis of patients with newly diagnosed
glioblastoma, PPI use was associated with inferior survival
outcomes. These findings suggest that PA-PPI use should be
discouraged in patients with glioblastoma, since alternative
agents are available and a detrimental effect cannot be
excluded. Translational research studies should explore
whether PPI-induced activity of ALDH mediates the potential
adverse effects of PPI in glioblastoma. .},
keywords = {Humans / Glioblastoma: mortality / Glioblastoma: drug
therapy / Proton Pump Inhibitors: therapeutic use / Male /
Female / Middle Aged / Aged / Adult / Brain Neoplasms:
mortality / Brain Neoplasms: drug therapy / Temozolomide:
therapeutic use / Proton Pump Inhibitors (NLM Chemicals) /
Temozolomide (NLM Chemicals)},
cin = {B320 / HD01},
ddc = {610},
cid = {I:(DE-He78)B320-20160331 / I:(DE-He78)HD01-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:41288972},
doi = {10.1001/jamanetworkopen.2025.45578},
url = {https://inrepo02.dkfz.de/record/306583},
}