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@ARTICLE{Song:286251,
author = {Y. Song and T. D. Kerr and C. Sanders and L. Dai and S. S.
Baxter and B. Somerville and R. N. Baugher and S. D. Mellott
and T. B. Young and H. E. Lawhorn and T. M. Plona and B. Xu
and L. Wei and Q. Hu and S. Liu and A. Hutson and B. Karim
and S. Burkett and S. Difilippantonio and L. Pinto and J.
Gebert and M. Kloor and S. M. Lipkin and S. Sei and R. H.
Shoemaker},
title = {{O}rganoids and metastatic orthotopic mouse model for
mismatch repair-deficient colorectal cancer.},
journal = {Frontiers in oncology},
volume = {13},
issn = {2234-943X},
address = {Lausanne},
publisher = {Frontiers Media},
reportid = {DKFZ-2023-02742},
pages = {1223915},
year = {2023},
abstract = {Genome integrity is essential for the survival of an
organism. DNA mismatch repair (MMR) genes (e.g., MLH1, MSH2,
MSH6, and PMS2) play a critical role in the DNA damage
response pathway for genome integrity maintenance. Germline
mutations of MMR genes can lead to Lynch syndrome or
constitutional mismatch repair deficiency syndrome,
resulting in an increased lifetime risk of developing cancer
characterized by high microsatellite instability (MSI-H) and
high mutation burden. Although immunotherapy has been
approved for MMR-deficient (MMRd) cancer patients, the
overall response rate needs to be improved and other
management options are needed.To better understand the
biology of MMRd cancers, elucidate the resistance mechanisms
to immune modulation, and develop vaccines and therapeutic
testing platforms for this high-risk population, we
generated organoids and an orthotopic mouse model from
intestine tumors developed in a Msh2-deficient mouse model,
and followed with a detailed characterization.The organoids
were shown to be of epithelial origin with stem cell
features, to have a high frameshift mutation frequency with
MSI-H and chromosome instability, and intra- and inter-tumor
heterogeneity. An orthotopic model using intra-cecal
implantation of tumor fragments derived from organoids
showed progressive tumor growth, resulting in the
development of adenocarcinomas mixed with mucinous features
and distant metastasis in liver and lymph node.The
established organoids with characteristics of MSI-H cancers
can be used to study MMRd cancer biology. The orthotopic
model, with its distant metastasis and expressing frameshift
peptides, is suitable for evaluating the efficacy of
neoantigen-based vaccines or anticancer drugs in combination
with other therapies.},
keywords = {Lynch syndrome (Other) / MSH2 (Other) / chromosome
instability (Other) / colorectal cancer (Other) /
microsatellite instability (Other) / mismatch repair
deficiency (Other) / mouse model (Other) / organoid (Other)},
cin = {F210},
ddc = {610},
cid = {I:(DE-He78)F210-20160331},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:37746286},
pmc = {pmc:PMC10516605},
doi = {10.3389/fonc.2023.1223915},
url = {https://inrepo02.dkfz.de/record/286251},
}