% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Bochtler:119318,
author = {T. Bochtler$^*$ and M. Granzow and F. Stölzel and C.
Kunz$^*$ and B. Mohr and M. Kartal-Kaess$^*$ and K.
Hinderhofer and C. Heilig$^*$ and M. Kramer and C. Thiede
and V. Endris and M. Kirchner$^*$ and A. Stenzinger and A.
Benner$^*$ and M. Bornhäuser and G. Ehninger and A. D. Ho
and A. Jauch and A. Krämer$^*$},
title = {{M}arker chromosomes can arise from chromothripsis and
predict adverse prognosis in acute myeloid leukemia.},
journal = {Blood},
volume = {129},
number = {10},
issn = {1528-0020},
address = {Stanford, Calif.},
publisher = {HighWire Press},
reportid = {DKFZ-2017-00073},
pages = {1333-1342},
year = {2017},
abstract = {Metaphase karyotyping is an established diagnostic standard
in acute myeloid leukemia (AML) for risk stratification. One
of the cytogenetic findings in AML are structurally highly
abnormal marker chromosomes. In this study we have assessed
frequency, cytogenetic characteristics, prognostic impact
and underlying biological origin of marker chromosomes.
Given their inherent gross structural chromosomal damage, we
speculated that they may arise from chromothripsis, a
recently described phenomenon of chromosome fragmentation in
a single catastrophic event. In 2 large consecutive
prospective, randomized, multicenter, intensive chemotherapy
trials (AML96, AML2003) from the Study Alliance Leukemia
(SAL) marker chromosomes were detectable in 165/1026
$(16.1\%)$ of aberrant non-core-binding-factor (CBF)
karyotype patients. Adverse-risk karyotypes displayed a
higher frequency of marker chromosomes $(26.5\%$ in
adverse-risk, $40.3\%$ in complex aberrant and $41.2\%$ in
abnormality(17p) karyotypes, p<.0001 each). Marker
chromosomes were associated with a poorer prognosis compared
to other non-CBF aberrant karyotypes and led to lower
remission rates (CR+CRi), inferior event-free survival as
well as overall survival in both trials. In multivariate
analysis, marker chromosomes independently predicted poor
prognosis in the AML96 trial ≤60 years. As detected by
array-CGH, about one third of marker chromosomes (18/49) had
arisen from chromothripsis, whereas this phenomenon was
virtually undetectable in a control group of marker
chromosome-negative complex aberrant karyotypes (1/34). The
chromothripsis-positive cases were characterized by a
particularly high degree of karyotype complexity, TP53
mutations and dismal prognosis. In conclusion, marker
chromosomes are indicative of chromothripsis and associated
with poor prognosis per se and not merely by association
with other adverse cytogenetic features.},
cin = {G330 / C060},
ddc = {610},
cid = {I:(DE-He78)G330-20160331 / I:(DE-He78)C060-20160331},
pnm = {317 - Translational cancer research (POF3-317)},
pid = {G:(DE-HGF)POF3-317},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:28119329},
doi = {10.1182/blood-2016-09-738161},
url = {https://inrepo02.dkfz.de/record/119318},
}