% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Bochtler:125525,
author = {T. Bochtler$^*$ and U. Hegenbart and C. Kunz$^*$ and A.
Benner$^*$ and C. Kimmich and A. Seckinger and D. Hose and
H. Goldschmidt and M. Granzow and P. Dreger and A. D. Ho and
A. Jauch and S. O. Schönland},
title = {{P}rognostic impact of cytogenetic aberrations in {AL}
amyloidosis patients after high-dose melphalan: a long-term
follow-up study.},
journal = {Blood},
volume = {128},
number = {4},
issn = {1528-0020},
address = {Stanford, Calif.},
publisher = {HighWire Press},
reportid = {DKFZ-2017-01651},
pages = {594 - 602},
year = {2016},
abstract = {Cytogenetic aberrations detected by interphase fluorescence
in situ hybridization (iFISH) of plasma cells are routinely
evaluated as prognostic markers in multiple myeloma. This
long-term follow-up study aimed to assess the prognosis of
systemic light chain amyloidosis (AL) patients treated with
high-dose melphalan (HDM) chemotherapy and autologous stem
cell transplantation, depending on iFISH results. Therefore,
we analyzed a consecutive cohort of 123 AL patients
recruited from 2003 to 2014. HDM was safe, with only 1 of
123 patients dying as a result of treatment-related
mortality, and effective, with a complete remission (CR)
rate of $34\%.$ Translocation t(11;14) as the most prevalent
aberration $(59\%)$ led to an improved CR rate after
high-dose therapy $(41.2\%$ vs $20.0\%;$ P = .02),
translating into a prolonged hematologic event-free survival
(hemEFS; median, 46.1 vs 28.1 months; P = .05) and a trend
for better overall survival (median, not reached vs 93.7
months; P = .07). In multivariate analysis, t(11;14) was
confirmed as a favorable prognostic factor regarding hemEFS
along with lower values for the difference between involved
and uninvolved free light chains. Conversely, deletion
13q14, gain of 1q21, and hyperdiploidy had no significant
prognostic impact. The high-risk cytogenetic aberrations
t(4;14), t(14;16), and del(17p13) conferred an unfavorable
prognosis, although statistical significance was reached
only for univariate CR analysis in this small group of 9
patients. Thus, t(11;14) positivity in HDM-treated AL
patients conferred superior CR rates and hemEFS. In view of
the reduced response of t(11;14) to bortezomib, this
highlights the impact of therapy on the prognostic role of
cytogenetic aberrations.},
keywords = {Immunoglobulin Light Chains (NLM Chemicals) / Melphalan
(NLM Chemicals)},
cin = {G330 / C060},
ddc = {610},
cid = {I:(DE-He78)G330-20160331 / I:(DE-He78)C060-20160331},
pnm = {317 - Translational cancer research (POF3-317)},
pid = {G:(DE-HGF)POF3-317},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:27257181},
doi = {10.1182/blood-2015-10-676361},
url = {https://inrepo02.dkfz.de/record/125525},
}