000125616 001__ 125616 000125616 005__ 20240228143319.0 000125616 0247_ $$2doi$$a10.1200/JCO.2015.66.0001 000125616 0247_ $$2pmid$$apmid:27432915 000125616 0247_ $$2pmc$$apmc:PMC5505170 000125616 0247_ $$2ISSN$$a0732-183X 000125616 0247_ $$2ISSN$$a1527-7755 000125616 0247_ $$2altmetric$$aaltmetric:9844322 000125616 037__ $$aDKFZ-2017-01742 000125616 041__ $$aeng 000125616 082__ $$a050 000125616 1001_ $$aChagtai, Tasnim$$b0 000125616 245__ $$aGain of 1q As a Prognostic Biomarker in Wilms Tumors (WTs) Treated With Preoperative Chemotherapy in the International Society of Paediatric Oncology (SIOP) WT 2001 Trial: A SIOP Renal Tumours Biology Consortium Study. 000125616 260__ $$aAlexandria, Va.$$bAmerican Society of Clinical Oncology$$c2016 000125616 3367_ $$2DRIVER$$aarticle 000125616 3367_ $$2DataCite$$aOutput Types/Journal article 000125616 3367_ $$0PUB:(DE-HGF)16$$2PUB:(DE-HGF)$$aJournal Article$$bjournal$$mjournal$$s1521723162_2108 000125616 3367_ $$2BibTeX$$aARTICLE 000125616 3367_ $$2ORCID$$aJOURNAL_ARTICLE 000125616 3367_ $$00$$2EndNote$$aJournal Article 000125616 520__ $$aWilms tumor (WT) is the most common pediatric renal tumor. Treatment planning under International Society of Paediatric Oncology (SIOP) protocols is based on staging and histologic assessment of response to preoperative chemotherapy. Despite high overall survival (OS), many relapses occur in patients without specific risk factors, and many successfully treated patients are exposed to treatments with significant risks of late effects. To investigate whether molecular biomarkers could improve risk stratification, we assessed 1q status and other potential copy number biomarkers in a large WT series.WT nephrectomy samples from 586 SIOP WT 2001 patients were analyzed using a multiplex ligation-dependent probe amplification (MLPA) assay that measured the copy number of 1q and other regions of interest.One hundred sixty-seven (28%) of 586 WTs had 1q gain. Five-year event-free survival (EFS) was 75.0% in patients with 1q gain (95% CI, 68.5% to 82.0%) and 88.2% in patients without gain (95% CI, 85.0% to 91.4%). OS was 88.4% with gain (95% CI, 83.5% to 93.6%) and 94.4% without gain (95% CI, 92.1% to 96.7%). In univariable analysis, 1q gain was associated with poorer EFS (P < .001; hazard ratio, 2.33) and OS (P = .01; hazard ratio, 2.16). The association of 1q gain with poorer EFS retained significance in multivariable analysis adjusted for 1p and 16q loss, sex, stage, age, and histologic risk group. Gain of 1q remained associated with poorer EFS in tumor subsets limited to either intermediate-risk localized disease or nonanaplastic localized disease. Other notable aberrations associated with poorer EFS included MYCN gain and TP53 loss.Gain of 1q is a potentially valuable prognostic biomarker in WT, in addition to histologic response to preoperative chemotherapy and tumor stage. 000125616 536__ $$0G:(DE-HGF)POF3-312$$a312 - Functional and structural genomics (POF3-312)$$cPOF3-312$$fPOF III$$x0 000125616 588__ $$aDataset connected to CrossRef, PubMed, 000125616 650_7 $$2NLM Chemicals$$aBiomarkers, Tumor 000125616 7001_ $$aZill, Christina$$b1 000125616 7001_ $$aDainese, Linda$$b2 000125616 7001_ $$aWegert, Jenny$$b3 000125616 7001_ $$aSavola, Suvi$$b4 000125616 7001_ $$aPopov, Sergey$$b5 000125616 7001_ $$aMifsud, William$$b6 000125616 7001_ $$aVujanić, Gordan$$b7 000125616 7001_ $$aSebire, Neil$$b8 000125616 7001_ $$aLe Bouc, Yves$$b9 000125616 7001_ $$aAmbros, Peter F$$b10 000125616 7001_ $$aKager, Leo$$b11 000125616 7001_ $$aO'Sullivan, Maureen J$$b12 000125616 7001_ $$aBlaise, Annick$$b13 000125616 7001_ $$aBergeron, Christophe$$b14 000125616 7001_ $$aMengelbier, Linda Holmquist$$b15 000125616 7001_ $$aGisselsson, David$$b16 000125616 7001_ $$0P:(DE-He78)4c28e2aade5f44d8eca9dd8e97638ec8$$aKool, Marcel$$b17$$udkfz 000125616 7001_ $$aTytgat, Godelieve A M$$b18 000125616 7001_ $$avan den Heuvel-Eibrink, Marry M$$b19 000125616 7001_ $$aGraf, Norbert$$b20 000125616 7001_ $$avan Tinteren, Harm$$b21 000125616 7001_ $$aCoulomb, Aurore$$b22 000125616 7001_ $$aGessler, Manfred$$b23 000125616 7001_ $$aWilliams, Richard Dafydd$$b24 000125616 7001_ $$aPritchard-Jones, Kathy$$b25 000125616 773__ $$0PERI:(DE-600)2005181-5$$a10.1200/JCO.2015.66.0001$$gVol. 34, no. 26, p. 3195 - 3203$$n26$$p3195 - 3203$$tJournal of clinical oncology$$v34$$x1527-7755$$y2016 000125616 909CO $$ooai:inrepo02.dkfz.de:125616$$pVDB 000125616 9101_ $$0I:(DE-588b)2036810-0$$6P:(DE-He78)4c28e2aade5f44d8eca9dd8e97638ec8$$aDeutsches Krebsforschungszentrum$$b17$$kDKFZ 000125616 9131_ $$0G:(DE-HGF)POF3-312$$1G:(DE-HGF)POF3-310$$2G:(DE-HGF)POF3-300$$3G:(DE-HGF)POF3$$4G:(DE-HGF)POF$$aDE-HGF$$bGesundheit$$lKrebsforschung$$vFunctional and structural genomics$$x0 000125616 9141_ $$y2016 000125616 915__ $$0StatID:(DE-HGF)0420$$2StatID$$aNationallizenz 000125616 915__ $$0StatID:(DE-HGF)0100$$2StatID$$aJCR$$bJ CLIN ONCOL : 2015 000125616 915__ $$0StatID:(DE-HGF)0200$$2StatID$$aDBCoverage$$bSCOPUS 000125616 915__ $$0StatID:(DE-HGF)0300$$2StatID$$aDBCoverage$$bMedline 000125616 915__ $$0StatID:(DE-HGF)0310$$2StatID$$aDBCoverage$$bNCBI Molecular Biology Database 000125616 915__ $$0StatID:(DE-HGF)0199$$2StatID$$aDBCoverage$$bThomson Reuters Master Journal List 000125616 915__ $$0StatID:(DE-HGF)0110$$2StatID$$aWoS$$bScience Citation Index 000125616 915__ $$0StatID:(DE-HGF)0150$$2StatID$$aDBCoverage$$bWeb of Science Core Collection 000125616 915__ $$0StatID:(DE-HGF)0111$$2StatID$$aWoS$$bScience Citation Index Expanded 000125616 915__ $$0StatID:(DE-HGF)1110$$2StatID$$aDBCoverage$$bCurrent Contents - Clinical Medicine 000125616 915__ $$0StatID:(DE-HGF)1030$$2StatID$$aDBCoverage$$bCurrent Contents - Life Sciences 000125616 915__ $$0StatID:(DE-HGF)9920$$2StatID$$aIF >= 20$$bJ CLIN ONCOL : 2015 000125616 9201_ $$0I:(DE-He78)B062-20160331$$kB062$$lPädiatrische Neuroonkologie$$x0 000125616 980__ $$ajournal 000125616 980__ $$aVDB 000125616 980__ $$aI:(DE-He78)B062-20160331 000125616 980__ $$aUNRESTRICTED