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@ARTICLE{Inta:125990,
author = {I. M. Inta and D. Choukair and S. Bender$^*$ and C. Kneppo
and S. Knauer-Fischer and K. Meyenburg and B. Ivandic and S.
Pfister$^*$ and M. Bettendorf},
title = {{G}uanine nucleotide-binding protein α subunit
hypofunction in children with short stature and
disproportionate shortening of the 4th and 5th metacarpals.},
journal = {Hormone research in paediatrics},
volume = {81},
number = {3},
issn = {1663-2826},
address = {Basel},
publisher = {Karger},
reportid = {DKFZ-2017-02105},
pages = {196 - 203},
year = {2014},
abstract = {GNAS encodes the α subunit of the stimulatory G protein
(Gsα). Maternal inherited Gsα mutations cause
pseudohypoparathyroidism type Ia (PHP-Ia), associated with
shortening of the 4th and 5th metacarpals.Here we
investigated the Gsα pathway in short patients with
distinct shortening of the 4th and 5th metacarpals.In 571
children with short stature and 4 patients with PHP-Ia
metacarpal bone lengths were measured. In identified
patients we analysed the Gsα protein function in platelets,
performed GNAS sequencing, and epigenetic analysis of four
significant differentially methylated regions.In 51 patients
$(8.9\%)$ shortening of the 4th and 5th metacarpals was more
pronounced than their height deficit. No GNAS coding
mutations were identified in 20 analysed patients, except in
2 PHP-Ia patients. Gsα activity was reduced in all PHP-Ia
patients and in $25\%$ of the analysed patients. No
significant methylation changes were identified.Our findings
suggest that patients with short stature and distinct
metacarpal bone shortening could be part of the wide variety
of PHP/PPHP, therefore it was worthwhile analysing the Gsα
protein function and GNAS gene in these patients in order to
further elucidate the phenotype and genotype of Gsα
dysfunction.},
cin = {B062},
ddc = {610},
cid = {I:(DE-He78)B062-20160331},
pnm = {312 - Functional and structural genomics (POF3-312)},
pid = {G:(DE-HGF)POF3-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:24481334},
doi = {10.1159/000356928},
url = {https://inrepo02.dkfz.de/record/125990},
}