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@ARTICLE{HollandLetz:126744,
author = {T. Holland-Letz$^*$ and A. Kopp-Schneider$^*$},
title = {{O}ptimal experimental designs for dose-response studies
with continuous endpoints.},
journal = {Archives of toxicology},
volume = {89},
number = {11},
issn = {1432-0738},
address = {Berlin},
publisher = {Springer},
reportid = {DKFZ-2017-02772},
pages = {2059 - 2068},
year = {2015},
abstract = {In most areas of clinical and preclinical research, the
required sample size determines the costs and effort for any
project, and thus, optimizing sample size is of primary
importance. An experimental design of dose-response studies
is determined by the number and choice of dose levels as
well as the allocation of sample size to each level. The
experimental design of toxicological studies tends to be
motivated by convention. Statistical optimal design theory,
however, allows the setting of experimental conditions (dose
levels, measurement times, etc.) in a way which minimizes
the number of required measurements and subjects to obtain
the desired precision of the results. While the general
theory is well established, the mathematical complexity of
the problem so far prevents widespread use of these
techniques in practical studies. The paper explains the
concepts of statistical optimal design theory with a minimum
of mathematical terminology and uses these concepts to
generate concrete usable D-optimal experimental designs for
dose-response studies on the basis of three common
dose-response functions in toxicology: log-logistic,
log-normal and Weibull functions with four parameters each.
The resulting designs usually require control plus only
three dose levels and are quite intuitively plausible. The
optimal designs are compared to traditional designs such as
the typical setup of cytotoxicity studies for 96-well
plates. As the optimal design depends on prior estimates of
the dose-response function parameters, it is shown what loss
of efficiency occurs if the parameters for design
determination are misspecified, and how Bayes optimal
designs can improve the situation.},
cin = {C060},
ddc = {610},
cid = {I:(DE-He78)C060-20160331},
pnm = {313 - Cancer risk factors and prevention (POF3-313)},
pid = {G:(DE-HGF)POF3-313},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:25155192},
pmc = {pmc:PMC4655015},
doi = {10.1007/s00204-014-1335-2},
url = {https://inrepo02.dkfz.de/record/126744},
}