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@ARTICLE{Ketzer:127104,
author = {P. Ketzer$^*$ and J. K. Kaufmann$^*$ and S. Engelhardt$^*$
and S. Bossow$^*$ and C. von Kalle$^*$ and J. S. Hartig and
G. Ungerechts$^*$ and D. Nettelbeck$^*$},
title = {{A}rtificial riboswitches for gene expression and
replication control of {DNA} and {RNA} viruses.},
journal = {Proceedings of the National Academy of Sciences of the
United States of America},
volume = {111},
number = {5},
issn = {1091-6490},
address = {Washington, DC},
publisher = {National Acad. of Sciences},
reportid = {DKFZ-2017-03130},
pages = {E554 - E562},
year = {2014},
abstract = {Aptazymes are small, ligand-dependent self-cleaving
ribozymes that function independently of transcription
factors and can be customized for induction by various small
molecules. Here, we introduce these artificial riboswitches
for regulation of DNA and RNA viruses. We hypothesize that
they represent universally applicable tools for studying
viral gene functions and for applications as a safety switch
for oncolytic and live vaccine viruses. Our study shows that
the insertion of artificial aptazymes into the adenoviral
immediate early gene E1A enables small-molecule-triggered,
dose-dependent inhibition of gene expression.
Aptazyme-mediated shutdown of E1A expression translates into
inhibition of adenoviral genome replication, infectious
particle production, and cytotoxicity/oncolysis. These
results provide proof of concept for the aptazyme approach
for effective control of biological outcomes in eukaryotic
systems, specifically in virus infections. Importantly, we
also demonstrate aptazyme-dependent regulation of measles
virus fusion protein expression, translating into potent
reduction of progeny infectivity and virus spread. This not
only establishes functionality of aptazymes in fully
cytoplasmic genetic systems, but also implicates general
feasibility of this strategy for application in viruses with
either DNA or RNA genomes. Our study implies that gene
regulation by artificial riboswitches may be an appealing
alternative to Tet- and other protein-dependent gene
regulation systems, based on their small size, RNA-intrinsic
mode of action, and flexibility of the inducing molecule.
Future applications range from gene analysis in basic
research to medicine, for example as a safety switch for new
generations of efficiency-enhanced oncolytic viruses.},
keywords = {Adenovirus E1A Proteins (NLM Chemicals) / Ligands (NLM
Chemicals) / RNA, Catalytic (NLM Chemicals) / Riboswitch
(NLM Chemicals)},
cin = {F110 / G100},
ddc = {000},
cid = {I:(DE-He78)F110-20160331 / I:(DE-He78)G100-20160331},
pnm = {316 - Infections and cancer (POF3-316)},
pid = {G:(DE-HGF)POF3-316},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:24449891},
pmc = {pmc:PMC3918795},
doi = {10.1073/pnas.1318563111},
url = {https://inrepo02.dkfz.de/record/127104},
}