% IMPORTANT: The following is UTF-8 encoded. This means that in the presence % of non-ASCII characters, it will not work with BibTeX 0.99 or older. % Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or % “biber”. @ARTICLE{Mai:129105, author = {E. K. Mai and A. Benner$^*$ and U. Bertsch and P. Brossart and A. Hänel and V. Kunzmann and R. Naumann and K. Neben and G. Egerer and A. D. Ho and J. Hillengass and M. S. Raab$^*$ and A. Neubauer and A. Peyn and Y.-D. Ko and N. Peter and C. Scheid and H. Goldschmidt$^*$}, title = {{S}ingle versus tandem high-dose melphalan followed by autologous blood stem cell transplantation in multiple myeloma: long-term results from the phase {III} {GMMG}-{HD}2 trial.}, journal = {British journal of haematology}, volume = {173}, number = {5}, issn = {0007-1048}, address = {Oxford [u.a.]}, publisher = {Wiley-Blackwell55962}, reportid = {DKFZ-2017-05110}, pages = {731 - 741}, year = {2016}, abstract = {The prospective, randomized phase III trial GMMG-HD2 aimed at demonstrating non-inferiority of single (Arm A) versus tandem (Arm B) high-dose melphalan followed by autologous transplantation (HDM/ASCT) with regard to 2-year event-free survival (EFS) in newly-diagnosed multiple myeloma (MM) and included 358 evaluable patients [Intention-to-treat population, (ITT), single/tandem HDM/ASCT: n = 177/181]. After a median follow-up of more than 11 years, non-inferiority of single versus tandem HDM/ASCT was demonstrated using the planned non-inferiority threshold of $15\%$ of the 2-year EFS rate. Neither EFS (P = 0·53) nor overall survival (OS) (P = 0·33) differences were observed in the ITT population. In the tandem arm, $26\%$ (n = 47/181) of patients refused a second HDM/ASCT due to non-medical reasons. A per-protocol (PP) analysis, including patients who received the intervention (single/tandem HDM/ASCT: n = 156/93) and patients who did not receive a second HDM/ASCT due to medical reasons $(12\%,$ n = 22/181), did not yield differences in EFS (P = 0·61) or OS (P = 0·16). In the ITT and PP set of the tandem arm, the rates of complete responses increased from first to second HDM/ASCT (both P = 0·04). Ten-year OS for the entire ITT was $34\%$ $(95\%$ confidence interval: $29-40\%).$ OS after first relapse was significantly shortened in the tandem arm (P = 0·04). In this study single HDM/ASCT was non-inferior to tandem HDM/ASCT in MM.}, keywords = {Myeloablative Agonists (NLM Chemicals) / Melphalan (NLM Chemicals)}, cin = {G330 / C060 / G170 / V964}, ddc = {610}, cid = {I:(DE-He78)G330-20160331 / I:(DE-He78)C060-20160331 / I:(DE-He78)G170-20160331 / I:(DE-He78)V964-20160331}, pnm = {317 - Translational cancer research (POF3-317)}, pid = {G:(DE-HGF)POF3-317}, typ = {PUB:(DE-HGF)16}, pubmed = {pmid:26990892}, doi = {10.1111/bjh.13994}, url = {https://inrepo02.dkfz.de/record/129105}, }