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@ARTICLE{Sananes:136966,
author = {A. Sananes and I. Cohen and A. Shahar and A. Hockla and E.
De Vita$^*$ and A. Miller$^*$ and E. S. Radisky and N. Papo},
title = {{A} potent, proteolysis-resistant inhibitor of
kallikrein-related peptidase 6 ({KLK}6) for cancer therapy,
developed by combinatorial engineering.},
journal = {The journal of biological chemistry},
volume = {293},
number = {33},
issn = {1083-351X},
address = {Bethesda, Md.},
publisher = {Soc.},
reportid = {DKFZ-2018-01395},
pages = {12663 - 12680},
year = {2018},
abstract = {Human tissue kallikrein (KLK) proteases are hormone-like
signaling molecules with important functions in cancer
pathophysiology. KLK-related peptidase 6 (KLK6),
specifically, is highly up-regulated in several types of
cancer, where its increased activity promotes cancer
invasion and metastasis. This characteristic suggests KLK6
as an attractive target for therapeutic interventions.
However, inhibitors that specifically target KLK6 have not
yet been reported, possibly because KLK6 shares a high
sequence homology and structural similarity with other
serine proteases and resists inhibition by many polypeptide
inhibitors. Here, we present an innovative combinatorial
approach to engineering KLK6 inhibitors via flow
cytometry-based screening of a yeast-displayed mutant
library of the human amyloid precursor protein Kunitz
protease inhibitor domain (APPI), an inhibitor of other
serine proteases, such as anionic and cationic trypsins. On
the basis of this screening, we generated
APPIM17L,I18F,S19F,F34V (APPI-4M), an APPI variant with a
KLK6 inhibition constant (Ki ) of 160 pm and a turnover time
of 10 days. To the best of our knowledge, APPI-4M is the
most potent KLK6 inhibitor reported to date, displaying
146-fold improved affinity and 13-fold improved proteolytic
stability compared with WT APPI (APPIWT). We further
demonstrate that APPI-4M acts as a functional inhibitor in a
cell-based model of KLK6-dependent breast cancer invasion.
Finally, the crystal structures of the APPIWT/KLK6 and
APPI-4M/KLK6 complexes revealed the structural and
mechanistic bases for the improved KLK6 binding and
proteolytic resistance of APPI-4M. We anticipate that
APPI-4M will have substantial translational potential as
both imaging agent and therapeutic.},
cin = {G404},
ddc = {570},
cid = {I:(DE-He78)G404-20160331},
pnm = {317 - Translational cancer research (POF3-317)},
pid = {G:(DE-HGF)POF3-317},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:29934309},
pmc = {pmc:PMC6102146},
doi = {10.1074/jbc.RA117.000871},
url = {https://inrepo02.dkfz.de/record/136966},
}