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@ARTICLE{Leeksma:142962,
author = {A. C. Leeksma and J. Taylor and B. Wu$^*$ and J. R. Gardner
and J. He and M. Nahas and M. Gonen and W. G. Alemayehu and
D. Te Raa and T. Walther$^*$ and J. Hüllein$^*$ and S.
Dietrich and R. Claus and F. de Boer and K. de Heer and J.
Dubois and M. Dampmann and J. Dürig and M. H. J. van Oers
and C. H. Geisler and E. Eldering and R. L. Levine and V.
Miller and T. Mughal and N. Lamanna and M. G. Frattini and
M. L. Heaney and A. Zelenetz and T. Zenz$^*$ and O.
Abdel-Wahab and A. P. Kater},
title = {{C}lonal diversity predicts adverse outcome in chronic
lymphocytic leukemia.},
journal = {Leukemia},
volume = {33},
number = {2},
issn = {1476-5551},
address = {London},
publisher = {Springer Nature},
reportid = {DKFZ-2019-00590},
pages = {390 - 402},
year = {2019},
abstract = {Genomic analyses of chronic lymphocytic leukemia (CLL)
identified somatic mutations and associations of clonal
diversity with adverse outcomes. Clonal evolution likely has
therapeutic implications but its dynamic is less well
studied. We studied clonal composition and prognostic value
of seven recurrently mutated driver genes using targeted
next-generation sequencing in 643 CLL patients and found
higher frequencies of mutations in TP53 (35 vs. $12\%,$
p < 0.001) and SF3B1 (20 vs. $11\%,$ p < 0.05) and
increased number of (sub)clonal (p < 0.0001) mutations
in treated patients. We next performed an in-depth
evaluation of clonal evolution on untreated CLL patients (50
'progressors' and 17 matched 'non-progressors') using a 404
gene-sequencing panel and identified novel mutated genes
such as AXIN1, SDHA, SUZ12, and FOXO3. Progressors carried
more mutations at initial presentation (2.5 vs. 1,
p < 0.0001). Mutations in specific genes were associated
with increased (SF3B1, ATM, and FBXW7) or decreased
progression risk (AXIN1 and MYD88). Mutations affecting
specific signaling pathways, such as Notch and MAP kinase
pathway were enriched in progressive relative to
non-progressive patients. These data extend earlier findings
that specific genomic alterations and diversity of subclones
are associated with disease progression and persistence of
disease in CLL and identify novel recurrently mutated genes
and associated outcomes.},
cin = {G250},
ddc = {610},
cid = {I:(DE-He78)G250-20160331},
pnm = {312 - Functional and structural genomics (POF3-312)},
pid = {G:(DE-HGF)POF3-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:30038380},
doi = {10.1038/s41375-018-0215-9},
url = {https://inrepo02.dkfz.de/record/142962},
}