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@ARTICLE{Schlenk:154483,
author = {R. F. Schlenk and P. Paschka and J. Krzykalla$^*$ and D.
Weber and S. Kapp-Schwoerer and V. I. Gaidzik and C. Leis
and W. Fiedler and T. Kindler and T. Schroeder and K. Mayer
and M. Lübbert and M. Wattad and K. Götze and H. A. Horst
and E. Koller and G. Wulf and J. Schleicher and M. Bentz and
R. Greil and B. Hertenstein and J. Krauter and U. Martens
and D. Nachbaur and M. Abu Samra and M. Girschikofsky and N.
Basara and A. Benner and F. Thol and M. Heuser and A. Ganser
and K. Döhner and H. Döhner},
title = {{G}emtuzumab {O}zogamicin in {NPM}1-{M}utated {A}cute
{M}yeloid {L}eukemia: {E}arly {R}esults {F}rom the
{P}rospective {R}andomized {AMLSG} 09-09 {P}hase {III}
{S}tudy.},
journal = {Journal of clinical oncology},
volume = {38},
number = {6},
issn = {1527-7755},
address = {Alexandria, Va.},
publisher = {American Society of Clinical Oncology},
reportid = {DKFZ-2020-00805},
pages = {623 - 632},
year = {2020},
abstract = {High CD33 expression in acute myeloid leukemia (AML) with
mutated NPM1 provides a rationale for the evaluation of
gemtuzumab ozogamicin (GO) in this AML entity. We conducted
a randomized trial to evaluate GO in combination with
intensive induction and consolidation therapy in
NPM1-mutated AML.Between May 2010 and September 2017,
patients ≥ 18 years old and considered eligible for
intensive therapy were randomly assigned up front for
induction therapy with idarubicin, cytarabine, etoposide,
and all-trans-retinoic acid with or without GO. The early (P
= .02) primary end point of event-free survival (EFS) was
evaluated 6 months after completion of patient
recruitment.Five hundred eighty-eight patients were randomly
assigned (standard arm, n = 296; GO arm, n = 292). EFS in
the GO arm was not significantly different compared with
that in the standard arm (hazard ratio, 0.83; $95\%$ CI,
0.65 to 1.04; P = .10). The early death rate during
induction therapy was $10.3\%$ in the GO arm and $5.7\%$ in
the standard arm (P = .05). Causes of death in both arms
were mainly infections. The cumulative incidence of relapse
(CIR) in patients achieving a complete remission (CR) or CR
with incomplete hematologic recovery (CRi) was significantly
reduced in the GO arm compared with the standard arm (P =
.005), with no difference in the cumulative incidence of
death (P = .80). Subgroup analysis revealed a significant
beneficial effect of GO in female, younger (≤ 70 years),
and FLT3 internal tandem duplication-negative patients with
respect to EFS and CIR.The trial did not meet its early
primary end point of EFS, mainly as a result of a higher
early death rate in the GO arm. However, in patients
achieving CR/CRi after induction therapy, significantly
fewer relapses occurred in the GO compared with the standard
arm.},
cin = {C060},
ddc = {610},
cid = {I:(DE-He78)C060-20160331},
pnm = {313 - Cancer risk factors and prevention (POF3-313)},
pid = {G:(DE-HGF)POF3-313},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:31851556},
pmc = {pmc:PMC7030890},
doi = {10.1200/JCO.19.01406},
url = {https://inrepo02.dkfz.de/record/154483},
}