% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Coltin:170386,
author = {H. Coltin and L. Sundaresan and K. S. Smith and P. Skowron
and L. Massimi and C. G. Eberhart and K. C. Schreck and N.
Gupta and W. A. Weiss and D. Tirapelli and C. Carlotti and
K. K. W. Li and M. Ryzhova and A. Golanov and O. Zheludkova
and O. Absalyamova and K. Okonechnikov$^*$ and D.
Stichel$^*$ and A. von Deimling$^*$ and C. Giannini and S.
Raskin and E. G. Van Meir and J. A. Chan and D. Fults and L.
B. Chambless and S.-K. Kim and A. Vasiljevic and C.
Faure-Conter and R. Vibhakar and S. Jung and S. Leary and J.
Mora and R. E. McLendon and I. F. Pollack and P. Hauser and
W. A. Grajkowska and J. B. Rubin and M. C. van Veelen and P.
J. French and J. M. Kros and L. M. Liau and S. M.
Pfister$^*$ and M. Kool$^*$ and N. Kijima and M. D. Taylor
and R. J. Packer and P. A. Northcott and A. Korshunov$^*$
and V. Ramaswamy},
title = {{S}ubgroup and subtype-specific outcomes in adult
medulloblastoma.},
journal = {Acta neuropathologica},
volume = {142},
number = {5},
issn = {1432-0533},
address = {Heidelberg},
publisher = {Springer},
reportid = {DKFZ-2021-01895},
pages = {859-871},
year = {2021},
note = {#LA:B300# / 2021 Nov;142(5):859-871},
abstract = {Medulloblastoma, a common pediatric malignant central
nervous system tumour, represent a small proportion of brain
tumours in adults. Previously it has been shown that in
adults, Sonic Hedgehog (SHH)-activated tumours predominate,
with Wingless-type (WNT) and Group 4 being less common, but
molecular risk stratification remains a challenge. We
performed an integrated analysis consisting of genome-wide
methylation profiling, copy number profiling, somatic
nucleotide variants and correlation of clinical variables
across a cohort of 191 adult medulloblastoma cases
identified through the Medulloblastoma Advanced Genomics
International Consortium. We identified 30 WNT, 112 SHH, 6
Group 3, and 41 Group 4 tumours. Patients with SHH tumours
were significantly older at diagnosis compared to other
subgroups (p < 0.0001). Five-year progression-free survival
(PFS) for WNT, SHH, Group 3, and Group 4 tumours was 64.4
(48.0-86.5), $61.9\%$ (51.6-74.2), $80.0\%$ $(95\%$ CI
51.6-100.0), and $44.9\%$ $(95\%$ CI 28.6-70.7),
respectively (p = 0.06). None of the clinical variables
(age, sex, metastatic status, extent of resection,
chemotherapy, radiotherapy) were associated with
subgroup-specific PFS. Survival among patients with SHH
tumours was significantly worse for cases with chromosome 3p
loss (HR 2.9, $95\%$ CI 1.1-7.6; p = 0.02), chromosome 10q
loss (HR 4.6, $95\%$ CI 2.3-9.4; p < 0.0001), chromosome 17p
loss (HR 2.3, $95\%$ CI 1.1-4.8; p = 0.02), and PTCH1
mutations (HR 2.6, $95\%$ CI 1.1-6.2; p = 0.04). The
prognostic significance of 3p loss and 10q loss persisted in
multivariable regression models. For Group 4 tumours,
chromosome 8 loss was strongly associated with improved
survival, which was validated in a non-overlapping cohort
(combined cohort HR 0.2, $95\%$ CI 0.1-0.7; p = 0.007).
Unlike in pediatric medulloblastoma, whole chromosome 11
loss in Group 4 and chromosome 14q loss in SHH was not
associated with improved survival, where MYCN, GLI2 and MYC
amplification were rare. In sum, we report unique
subgroup-specific cytogenetic features of adult
medulloblastoma, which are distinct from those in younger
patients, and correlate with survival disparities. Our
findings suggest that clinical trials that incorporate new
strategies tailored to high-risk adult medulloblastoma
patients are urgently needed.},
keywords = {Adult (Other) / DNA methylation profiling (Other) /
Medulloblastoma (Other) / Molecular groups (Other) / Risk
stratification (Other)},
cin = {B062 / B300},
ddc = {610},
cid = {I:(DE-He78)B062-20160331 / I:(DE-He78)B300-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:34409497},
doi = {10.1007/s00401-021-02358-4},
url = {https://inrepo02.dkfz.de/record/170386},
}