% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Jahn:181024,
author = {N. Jahn and E. Jahn and M. Saadati and L. Bullinger and R.
A. Larson and T. Ottone and S. Amadori and T. W. Prior and
J. M. Brandwein and F. R. Appelbaum and B. C. Medeiros and
M. S. Tallman and G. Ehninger and M. Heuser and A. Ganser
and C. Pallaud and I. Gathmann and J. Krzykalla$^*$ and A.
Benner$^*$ and C. D. Bloomfield and C. Thiede and R. M.
Stone and H. Döhner and K. Döhner},
title = {{G}enomic landscape of patients with {FLT}3-mutated acute
myeloid leukemia ({AML}) treated within the {CALGB}
10603/{RATIFY} trial.},
journal = {Leukemia},
volume = {36},
number = {9},
issn = {0887-6924},
address = {London},
publisher = {Springer Nature},
reportid = {DKFZ-2022-01731},
pages = {2218-2227},
year = {2022},
note = {2022 Sep;36(9):2218-2227},
abstract = {The aim of this study was to characterize the mutational
landscape of patients with FLT3-mutated acute myeloid
leukemia (AML) treated within the randomized CALGB
10603/RATIFY trial evaluating intensive chemotherapy plus
the multi-kinase inhibitor midostaurin versus placebo. We
performed sequencing of 262 genes in 475 patients: mutations
occurring concurrently with the FLT3-mutation were most
frequent in NPM1 $(61\%),$ DNMT3A $(39\%),$ WT1 $(21\%),$
TET2 $(12\%),$ NRAS $(11\%),$ RUNX1 $(11\%),$ PTPN11
$(10\%),$ and ASXL1 $(8\%)$ genes. To assess effects of
clinical and genetic features and their possible
interactions, we fitted random survival forests and
interpreted the resulting variable importance. Highest
prognostic impact was found for WT1 and NPM1 mutations,
followed by white blood cell count, FLT3 mutation type
(internal tandem duplications vs. tyrosine kinase domain
mutations), treatment (midostaurin vs. placebo), ASXL1
mutation, and ECOG performance status. When evaluating
two-fold variable combinations the most striking effects
were found for WT1:NPM1 (with NPM1 mutation abrogating the
negative effect of WT1 mutation), and for WT1:treatment
(with midostaurin exerting a beneficial effect in
WT1-mutated AML). This targeted gene sequencing study
provides important, novel insights into the genomic
background of FLT3-mutated AML including the prognostic
impact of co-mutations, specific gene-gene interactions, and
possible treatment effects of midostaurin.},
cin = {C060},
ddc = {610},
cid = {I:(DE-He78)C060-20160331},
pnm = {313 - Krebsrisikofaktoren und Prävention (POF4-313)},
pid = {G:(DE-HGF)POF4-313},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:35922444},
doi = {10.1038/s41375-022-01650-w},
url = {https://inrepo02.dkfz.de/record/181024},
}