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@ARTICLE{Donson:276332,
author = {A. M. Donson and K. C. Bertrand and K. A. Riemondy and D.
Gao and Y. Zhuang and B. Sanford and G. A. Norris and R. J.
Chapman and R. Fu and N. Willard and A. M. Griesinger and G.
R. de Sousa and V. Amani and E. Grimaldo and T. C. Hankinson
and F. Booker and M. Sill$^*$ and R. G. Grundy and K.
Pajtler$^*$ and D. W. Ellison and N. K. Foreman and T. A.
Ritzmann},
title = {{S}ignificant increase of high-risk chromosome 1q gain and
6q loss at recurrence in posterior fossa group {A}
ependymoma: a multicenter study.},
journal = {Neuro-Oncology},
volume = {25},
number = {10},
issn = {1522-8517},
address = {Oxford},
publisher = {Oxford Univ. Press},
reportid = {DKFZ-2023-01062},
pages = {1854-1867},
year = {2023},
note = {2023 Oct 3;25(10):1854-1867},
abstract = {Ependymoma (EPN) posterior fossa group A (PFA) has the
highest rate of recurrence and the worst prognosis of all
EPN molecular groups. At relapse, it is typically incurable
even with re-resection and re-irradiation. The biology of
recurrent PFA remains largely unknown, however, the
increasing use of surgery at first recurrence has now
provided access to clinical samples to facilitate a better
understanding of this.In this large longitudinal
international multicenter study, we examined matched samples
of primary and recurrent disease from PFA patients to
investigate the biology of recurrence.DNA methylome derived
copy number variants (CNVs) revealed large scale chromosome
gains and losses at recurrence. CNV changes were dominated
by chromosome 1q gain and/or 6q loss, both previously
identified as high-risk factors in PFA, which were present
in $23\%$ at presentation but increased to $61\%$ at 1 st
recurrence. Multivariate survival analyses of this cohort
showed that cases with 1q gain or 6q loss at 1 st recurrence
were significantly more likely to recur again.
Predisposition to 1q+/6q- CNV changes at recurrence
correlated with hypomethylation of
heterochromatin-associated DNA at presentation. Cellular and
molecular analyses revealed that 1q+/6q- PFA had
significantly higher proportions of proliferative
neuroepithelial undifferentiated progenitors and decreased
differentiated neoplastic subpopulations.This study provides
clinically and preclinically-actionable insights into the
biology of PFA recurrence. The hypomethylation
predisposition signature in PFA is a potential
risk-classifier for trial stratification. We show that the
cellular heterogeneity of PFAs evolves largely because of
genetic evolution of neoplastic cells.},
keywords = {chromosomal instability (Other) / ependymoma (Other) /
prognosis (Other) / recurrence (Other)},
cin = {B062 / HD01},
ddc = {610},
cid = {I:(DE-He78)B062-20160331 / I:(DE-He78)HD01-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:37246777},
doi = {10.1093/neuonc/noad096},
url = {https://inrepo02.dkfz.de/record/276332},
}