000277733 001__ 277733 000277733 005__ 20240229155021.0 000277733 0247_ $$2doi$$a10.1007/s00401-023-02608-7 000277733 0247_ $$2pmid$$apmid:37450044 000277733 0247_ $$2ISSN$$a0001-6322 000277733 0247_ $$2ISSN$$a1432-0533 000277733 0247_ $$2altmetric$$aaltmetric:151601467 000277733 037__ $$aDKFZ-2023-01450 000277733 041__ $$aEnglish 000277733 082__ $$a610 000277733 1001_ $$0P:(DE-He78)3fdc3623477264cb5d0e14f256dbfbb8$$aJohann, Pascal$$b0$$eFirst author$$udkfz 000277733 245__ $$aRecurrent atypical teratoid/rhabdoid tumors (AT/RT) reveal discrete features of progression on histology, epigenetics, copy number profiling, and transcriptomics. 000277733 260__ $$aHeidelberg$$bSpringer$$c2023 000277733 3367_ $$2DRIVER$$aarticle 000277733 3367_ $$2DataCite$$aOutput Types/Journal article 000277733 3367_ $$0PUB:(DE-HGF)16$$2PUB:(DE-HGF)$$aJournal Article$$bjournal$$mjournal$$s1693559932_4717 000277733 3367_ $$2BibTeX$$aARTICLE 000277733 3367_ $$2ORCID$$aJOURNAL_ARTICLE 000277733 3367_ $$00$$2EndNote$$aJournal Article 000277733 500__ $$a#EA:B062# / 2023 Sep;146(3):527-541 000277733 520__ $$aAtypical teratoid/rhabdoid tumors (AT/RT) are the most common malignant brain tumors manifesting in infancy. They split into four molecular types. The major three (AT/RT-SHH, AT/RT-TYR, and AT/RT-MYC) all carry mutations in SMARCB1, the fourth quantitatively smaller type is characterized by SMARCA4 mutations (AT/RT-SMARCA4). Molecular characteristics of disease recurrence or metastatic spread, which go along with a particularly dismal outcome, are currently unclear. Here, we investigated tumor tissue from 26 patients affected by AT/RT to identify signatures of recurrences in comparison with matched primary tumor samples. Microscopically, AT/RT recurrences demonstrated a loss of architecture and significantly enhanced mitotic activity as compared to their related primary tumors. Based on DNA methylation profiling, primary tumor and related recurrence were grossly similar, but three out of 26 tumors belonged to a different molecular type or subtype after second surgery compared to related primary lesions. Copy number variations (CNVs) differed in six cases, showing novel gains on chromosome 1q or losses of chromosome 10 in recurrences as the most frequent alterations. To consolidate these observations, our cohort was combined with a data set of unmatched primary and recurrent AT/RT, which demonstrated chromosome 1q gain and 10 loss in 18% (n = 7) and 11% (n = 4) of the recurrences (n = 38) as compared to 7% (n = 3) and 0% (n = 0) in the primary tumors (n = 44), respectively. Similar to the observations made by DNA methylation profiling, RNA sequencing of our cohort revealed AT/RT primary tumors and matched recurrences clustering closely together. However, a number of genes showed significantly altered expression in AT/RT-SHH recurrences. Many of them are known tumor driving growth factors, involved in embryonal development and tumorigenesis, or are cell-cycle-associated. Overall, our work identifies subtle molecular changes that occur in the course of the disease and that may help define novel therapeutic targets for AT/RT recurrences. 000277733 536__ $$0G:(DE-HGF)POF4-312$$a312 - Funktionelle und strukturelle Genomforschung (POF4-312)$$cPOF4-312$$fPOF IV$$x0 000277733 588__ $$aDataset connected to CrossRef, PubMed, , Journals: inrepo02.dkfz.de 000277733 650_7 $$2Other$$aAT/RT 000277733 650_7 $$2Other$$aDNA methylation 000277733 650_7 $$2Other$$aPediatric cancer 000277733 650_7 $$2Other$$aRNA sequencing 000277733 650_7 $$2Other$$aRecurrent tumor 000277733 650_7 $$2Other$$aRhabdoid tumor 000277733 7001_ $$aAltendorf, Lea$$b1 000277733 7001_ $$aEfremova, Emma-Maria$$b2 000277733 7001_ $$aHolsten, Till$$b3 000277733 7001_ $$aSteinbügl, Mona$$b4 000277733 7001_ $$aNemes, Karolina$$b5 000277733 7001_ $$aEckhardt, Alicia$$b6 000277733 7001_ $$aKresbach, Catena$$b7 000277733 7001_ $$aBockmayr, Michael$$b8 000277733 7001_ $$aKoch, Arend$$b9 000277733 7001_ $$aHaberler, Christine$$b10 000277733 7001_ $$aAntonelli, Manila$$b11 000277733 7001_ $$aDeSisto, John$$b12 000277733 7001_ $$aSchuhmann, Martin U$$b13 000277733 7001_ $$aHauser, Peter$$b14 000277733 7001_ $$aSiebert, Reiner$$b15 000277733 7001_ $$aBens, Susanne$$b16 000277733 7001_ $$0P:(DE-He78)4c28e2aade5f44d8eca9dd8e97638ec8$$aKool, Marcel$$b17$$udkfz 000277733 7001_ $$aGreen, Adam L$$b18 000277733 7001_ $$aHasselblatt, Martin$$b19 000277733 7001_ $$aFrühwald, Michael C$$b20 000277733 7001_ $$00000-0002-8731-1121$$aSchüller, Ulrich$$b21 000277733 773__ $$0PERI:(DE-600)1458410-4$$a10.1007/s00401-023-02608-7$$n3$$p527-541$$tActa neuropathologica$$v146$$x0001-6322$$y2023 000277733 909CO $$ooai:inrepo02.dkfz.de:277733$$pVDB 000277733 9101_ $$0I:(DE-588b)2036810-0$$6P:(DE-He78)3fdc3623477264cb5d0e14f256dbfbb8$$aDeutsches Krebsforschungszentrum$$b0$$kDKFZ 000277733 9101_ $$0I:(DE-588b)2036810-0$$6P:(DE-He78)4c28e2aade5f44d8eca9dd8e97638ec8$$aDeutsches Krebsforschungszentrum$$b17$$kDKFZ 000277733 9131_ $$0G:(DE-HGF)POF4-312$$1G:(DE-HGF)POF4-310$$2G:(DE-HGF)POF4-300$$3G:(DE-HGF)POF4$$4G:(DE-HGF)POF$$aDE-HGF$$bGesundheit$$lKrebsforschung$$vFunktionelle und strukturelle Genomforschung$$x0 000277733 9141_ $$y2023 000277733 915__ $$0StatID:(DE-HGF)3002$$2StatID$$aDEAL Springer$$d2022-11-29$$wger 000277733 915__ $$0StatID:(DE-HGF)3002$$2StatID$$aDEAL Springer$$d2022-11-29$$wger 000277733 915__ $$0StatID:(DE-HGF)1190$$2StatID$$aDBCoverage$$bBiological Abstracts$$d2022-11-29 000277733 915__ $$0StatID:(DE-HGF)0113$$2StatID$$aWoS$$bScience Citation Index Expanded$$d2022-11-29 000277733 915__ $$0StatID:(DE-HGF)0160$$2StatID$$aDBCoverage$$bEssential Science Indicators$$d2022-11-29 000277733 915__ $$0StatID:(DE-HGF)0100$$2StatID$$aJCR$$bACTA NEUROPATHOL : 2022$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0200$$2StatID$$aDBCoverage$$bSCOPUS$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0300$$2StatID$$aDBCoverage$$bMedline$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0600$$2StatID$$aDBCoverage$$bEbsco Academic Search$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0030$$2StatID$$aPeer Review$$bASC$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0199$$2StatID$$aDBCoverage$$bClarivate Analytics Master Journal List$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)1050$$2StatID$$aDBCoverage$$bBIOSIS Previews$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)0150$$2StatID$$aDBCoverage$$bWeb of Science Core Collection$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)1030$$2StatID$$aDBCoverage$$bCurrent Contents - Life Sciences$$d2023-10-21 000277733 915__ $$0StatID:(DE-HGF)9910$$2StatID$$aIF >= 10$$bACTA NEUROPATHOL : 2022$$d2023-10-21 000277733 9201_ $$0I:(DE-He78)B062-20160331$$kB062$$lB062 Pädiatrische Neuroonkologie$$x0 000277733 9201_ $$0I:(DE-He78)HD01-20160331$$kHD01$$lDKTK HD zentral$$x1 000277733 9200_ $$0I:(DE-He78)B062-20160331$$kB062$$lB062 Pädiatrische Neuroonkologie$$x0 000277733 980__ $$ajournal 000277733 980__ $$aVDB 000277733 980__ $$aI:(DE-He78)B062-20160331 000277733 980__ $$aI:(DE-He78)HD01-20160331 000277733 980__ $$aUNRESTRICTED