%0 Journal Article
%A Mayr, Lisa
%A Neyazi, Sina
%A Schwark, Kallen
%A Trissal, Maria
%A Beck, Alexander
%A Labelle, Jenna
%A Eder, Sebastian K
%A Weiler-Wichtl, Liesa
%A Marques, Joana G
%A de Biagi-Junior, Carlos A O
%A Lo Cascio, Costanza
%A Chapman, Owen
%A Sridhar, Sunita
%A Kenkre, Rishaan
%A Dutta, Aditi
%A Wang, Shanqing
%A Wang, Jessica
%A Hack, Olivia
%A Nascimento, Andrezza
%A Nguyen, Cuong M
%A Castellani, Sophia
%A Rozowsky, Jacob S
%A Groves, Andrew
%A Panditharatna, Eshini
%A Cruzeiro, Gustavo Alencastro Veiga
%A Haase, Rebecca D
%A Tabatabai, Kuscha
%A Madlener, Sibylle
%A Wadden, Jack
%A Adam, Tiffany
%A Kong, Seongbae
%A Miclea, Madeline
%A Patel, Tirth
%A Bruckner, Katharina
%A Senfter, Daniel
%A Lämmerer, Anna
%A Supko, Jeffrey
%A Guntner, Armin S
%A Palova, Hana
%A Neradil, Jakub
%A Stepien, Natalia
%A Lötsch-Gojo, Daniela
%A Berger, Walter
%A Leiss, Ulrike
%A Rosenmayr, Verena
%A Dorfer, Christian
%A Dieckmann, Karin
%A Peyrl, Andreas
%A Azizi, Amedeo A
%A Baumgartner, Alicia
%A Slaby, Ondrej
%A Pokorna, Petra
%A Clark, Louise M
%A Cameron, Amy
%A Nguyen, Quang-De
%A Wakimoto, Hiroaki
%A Dubois, Frank
%A Greenwald, Noah F
%A Bandopadhayay, Pratiti
%A Beroukhim, Rameen
%A Ligon, Keith
%A Kramm, Christof
%A Bronsema, Annika
%A Bailey, Simon
%A Stucklin, Ana Guerreiro
%A Mueller, Sabine
%A Skrypek, Mary
%A Martinez, Nina
%A Bowers, Daniel C
%A Jones, David
%A Jones, Chris
%A Jäger, Natalie
%A Sterba, Jaroslav
%A Müllauer, Leonhard
%A Haberler, Christine
%A Kumar-Sinha, Chandan
%A Chinnaiyan, Arul
%A Mody, Rajen
%A Chavez, Lukas
%A Furtner, Julia
%A Koschmann, Carl
%A Gojo, Johannes
%A Filbin, Mariella G
%T Effective targeting of PDGFRA-altered high-grade glioma with avapritinib.
%J Cancer cell
%V 43
%N 4
%@ 1535-6108
%C Cambridge, Mass.
%I Cell Press
%M DKFZ-2025-00771
%P 740-756.e8
%D 2025
%Z 2025 Apr 14;43(4):740-756.e8
%X PDGFRA is crucial to tumorigenesis and frequently genomically altered in high-grade glioma (HGG). In a comprehensive dataset of pediatric HGG (n = 261), we detect PDGFRA mutations and/or amplifications in 15
%K PDGFRA alteration (Other)
%K PDGFRA amplification (Other)
%K PDGFRA inhibitor (Other)
%K PDGFRA mutation (Other)
%K avapritinib (Other)
%K brain penetrance (Other)
%K diffuse midline glioma (Other)
%K glioblastoma (Other)
%K high-grade glioma (Other)
%K tyrosine kinase inhibitor (Other)
%F PUB:(DE-HGF)16
%9 Journal Article
%$ pmid:40086436
%R 10.1016/j.ccell.2025.02.018
%U https://inrepo02.dkfz.de/record/300325