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@ARTICLE{OssamiSaidy:301519,
author = {A. Ossami Saidy and C. Peczynski and C. Thieblemont and M.
Daskalakis and M. Wehrli and D. Beauvais and J. Finke and E.
Schorb and P. Vandenberghe and P. Berning and M. Stelljes
and F. Ayuk and R. Ram and M. Von Bonin and P. Dreger and W.
Bethge and A. Kuhnl and L. Jost and F. Stölzel and B. von
Tresckow$^*$ and C. Renner and S. Fuhrmann and J.-E.
Galimard and E. Michel and A. Bazarbachi and A. S. Balari
and N. Schmitz and B. Glass},
title = {{E}fficacy and safety of {CAR} {T}-cell therapy in patients
with primary or secondary {CNS} lymphoma: {A} study on
behalf of the {EBMT} and the {G}o{CART} coalition.},
journal = {HemaSphere},
volume = {9},
number = {5},
issn = {2572-9241},
address = {Hoboken},
publisher = {John Wiley $\&$ Sons Ltd.},
reportid = {DKFZ-2025-01056},
pages = {e70146},
year = {2025},
abstract = {Patients with relapsed or refractory (r/r) primary central
nervous system (CNS) lymphoma (PCNSL) or secondary central
nervous system (CNS) lymphoma (SCNSL) face a dismal
prognosis. They have been excluded from most clinical CAR
T-cell trials as investigators feared an increased risk for
severe immune effector cell-associated neurotoxicity
(ICANS). To investigate the potential of anti-CD19 CAR
T-cell therapy (CART) in such patients, we analyzed data of
100 patients with CNS manifestation treated with CART
between January 2018 and July 2023 and reported to European
Society for Blood and Marrow Transplantation. Median age was
62 years. Of patients, $58\%$ had failed ≥3 treatment
lines, and $40\%$ had received autologous stem-cell
transplantation before CART. Fifty-nine patients received
axicabtagene ciloleucel, 38 patients were treated with
tisagenlecleucel, three patients received other products. At
the time of CART, 67 patients had active CNS disease.
Overall and progression-free survival (PFS) at 24 months
were $37\%$ and $28\%.$ Relapse incidence (RI) at 24 months
was $59\%,$ whereas non-relapse mortality at 1 year was
$7\%.$ Cytokine release syndrome (CRS) and ICANS of any
grade occurred in $83\%$ and $42\%$ of patients,
respectively. CRS grade 3 occurred in 11 and ICANS grades
3-4 in 17 patients. Two patients died of neurotoxicity.
Elevated lactate dehydrogenase was an independent risk
factor for RI and PFS (hazard ratio [HR] 2.4, p = 0.003; HR:
1.9, p = 0.016). Patients with ECOG 2-3 had a significantly
increased risk for the development of ICANS (HR 2.68, p =
0.002). These data support the implementation of CART as
treatment for patients with r/r PCNSL and SCNSL.},
cin = {ED01},
ddc = {610},
cid = {I:(DE-He78)ED01-20160331},
pnm = {899 - ohne Topic (POF4-899)},
pid = {G:(DE-HGF)POF4-899},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:40400509},
pmc = {pmc:PMC12093105},
doi = {10.1002/hem3.70146},
url = {https://inrepo02.dkfz.de/record/301519},
}