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@ARTICLE{Kapp:302049,
author = {J. N. Kapp and W. P. R. Verdurmen and J. V. Schaefer and K.
Kopra and G. Nagy-Davidescu and E. Richard and M.-J. Nokin
and P. Ernst and R. Tamaskovic and M. Schwill and R. Degen
and C. Scholl$^*$ and D. Santamaria and A. Plückthun},
title = {{A} nucleotide-independent, pan-{RAS}-targeted {DARP}in
elicits anti-tumor activity in a multimodal manner.},
journal = {Molecular oncology},
volume = {nn},
issn = {1574-7891},
address = {Hoboken, NJ},
publisher = {John Wiley $\&$ Sons, Inc.},
reportid = {DKFZ-2025-01240},
pages = {nn},
year = {2025},
note = {epub},
abstract = {The KRAS oncoprotein is a frequent tumor driver in lung,
pancreatic, and colorectal cancers and has proven to be a
challenging pharmaceutical target. The first KRAS-targeted
therapeutics are now being tested in clinical trials but the
consequences of preferentially targeting the GDP or GTP
state of KRAS and the relevance of RAS nanoclustering have
remained unclear. Here we report a Designed Ankyrin Repeat
Protein (DARPin) that recognizes the RAS switch I/II region
with low nm affinity, independently of the nucleotide bound
(GDP- or GTP state). This DARPin, termed $'784_F5',$
occupies the effector recognition lobe, resulting in
interference with SOS-mediated activation, RAS downstream
effector interactions, and KRAS nanoclustering.
Consequently, this anti-RAS DARPin potently blocks
downstream signaling, leading to a strong reduction in
proliferation and anchorage-independent growth in
RAS-dependent cell lines. We showed that the expression of
$'784_F5',$ the pan-RAS, nucleotide-independent DARPin can
lead to tumor regression in a colorectal xenograft model
which may hold promise for further investigation and
development.},
keywords = {Designed Ankyrin Repeat Protein (Other) / RAS (Other) /
cancer (Other) / drug development (Other) / oncogene (Other)
/ small GTPase (Other)},
cin = {B290},
ddc = {610},
cid = {I:(DE-He78)B290-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:40517320},
doi = {DOI:10.1002/1878-0261.70061},
url = {https://inrepo02.dkfz.de/record/302049},
}