TY - JOUR
AU - Imle, Roland
AU - Blösel, Daniel
AU - Kommoss, Felix Karl-Friedrich
AU - Placke, Sara
AU - Stutheit-Zhao, Eric
AU - Blume, Christina
AU - Lupar, Dmitry
AU - Schmitt, Lukas
AU - Winter, Claudia
AU - Wagner, Lena
AU - von Eicke, Malte
AU - Walzer, Hannah
AU - Förderer, Julia
AU - Laier, Stephanie
AU - Hertwig, Michael
AU - Peterziel, Heike
AU - Oehme, Ina
AU - Scheuerman, Sophia
AU - Seitz, Christian
AU - Geyer, Florian H
AU - Cidre-Aranaz, Florencia
AU - Grünewald, Thomas
AU - Vokuhl, Christian
AU - Chudasama, Priya
AU - Scholl, Claudia
AU - Schmidt, Claudia
AU - Günther, Patrick
AU - Sill, Martin
AU - Jones, Kevin B
AU - Pfister, Stefan
AU - Autry, Robert
AU - Banito, Ana
TI - Somatic gene delivery faithfully recapitulates a molecular spectrum of high-risk sarcomas.
JO - Nature Communications
VL - 16
IS - 1
SN - 2041-1723
CY - [London]
PB - Springer Nature
M1 - DKFZ-2025-01243
SP - 5283
PY - 2025
N1 - DKFZ-ZMBH Alliance / #EA:B380#LA:B380#
AB - A major challenge hampering therapeutic advancements for high-risk sarcoma patients is the broad spectrum of molecularly distinct sarcoma types and the corresponding lack of suitable model systems. Here we describe the development of a genetically-controlled, yet versatile mouse modeling platform allowing delivery of different genetic lesions by muscle electroporation (EPO) in wildtype mice. This EPO-GEMM (EPO-based genetically engineered mouse model) platform allows the generation of ten genetically distinct sarcomas on an isogenic background, including the first model of ETV6::NTRK3-driven sarcoma. Comprehensive histological and molecular profiling reveals that this mouse sarcoma cohort recapitulates a spectrum of molecularly diverse sarcomas with gene fusions acting as major determinants of sarcoma biology. Integrative cross-species analyses show faithful recapitulation of human sarcoma subtypes, including expression of relevant immunotherapy targets. Comparison of syngeneic allografting methods enables reliable preservation and scalability of sarcoma-EPO-GEMMs for preclinical treatment trials, such as NTRK inhibitor therapy in an immunocompetent background.
KW - Animals
KW - Sarcoma: genetics
KW - Sarcoma: pathology
KW - Mice
KW - Humans
KW - Disease Models, Animal
KW - Gene Transfer Techniques
KW - Electroporation: methods
KW - Mice, Transgenic
KW - Female
KW - Mice, Inbred C57BL
LB - PUB:(DE-HGF)16
C6 - pmid:40523919
C2 - pmc:PMC12170903
DO - DOI:10.1038/s41467-025-60519-5
UR - https://inrepo02.dkfz.de/record/302111
ER -