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@ARTICLE{Aust:303097,
author = {O. Aust and M. R. T. Thiel and E. Blanc and M. Lüthen and
V. Hollek and R. Astaburuaga-García and B. Klinger and F.
Böhning and A. Trinks and D. Beule and B. Papke$^*$ and D.
Horst$^*$ and N. Blüthgen$^*$ and C. Sers$^*$ and C. J. Der
and M. Morkel$^*$},
title = {{R}eporter-based screening identifies {RAS}-{RAF} mutations
as drivers of resistance to active-state {RAS} inhibitors in
colorectal cancer.},
journal = {Science signaling},
volume = {18},
number = {896},
issn = {1945-0877},
address = {Washington, DC [u.a.]},
publisher = {Assoc.},
reportid = {DKFZ-2025-01522},
pages = {eadr3738},
year = {2025},
abstract = {Therapy-induced acquired resistance limits the clinical
effectiveness of mutation-specific KRAS inhibitors in
colorectal cancer (CRC). Here, we investigated whether
broad-spectrum, active-state RAS inhibitors meet similar
limitations. We found that KRAS-mutant CRC cell lines were
sensitive to the RAS(ON) multiselective RAS inhibitor
RMC-7977, given that treatment resulted in RAS-RAF-MEK-ERK
pathway inhibition; halted proliferation; and, in some
cases, induced apoptosis. RMC-7977 initially reduced the
activity of a compartment-specific, dual-color reporter of
ERK activity, with reporter reactivation emerging after
long-term dose escalation. These drug-resistant cell
populations exhibited distinct patterns of phospho-protein
abundance, transcriptional activities, and genomic
mutations, including a Y71H mutation in KRAS and an S257L
mutation in RAF1. Transgenic expression of KRASG13D, Y71H or
RAF1S257L in drug-sensitive CRC cells induced resistance to
RMC-7977. CRC cells that were resistant to RMC-7977 and
harboring RAF1S257L exhibited synergistic sensitivity to
concurrent inhibition of RAS and RAF. Our findings
demonstrate the power of reporter-assisted screening
together with single-cell analyses for dissecting the
complex landscape of therapy resistance. The strategy offers
opportunities to develop clinically relevant combinatorial
treatments to counteract the emergence of resistant cancer
cells.},
keywords = {Humans / Colorectal Neoplasms: genetics / Colorectal
Neoplasms: drug therapy / Colorectal Neoplasms: pathology /
Colorectal Neoplasms: metabolism / Drug Resistance,
Neoplasm: genetics / Drug Resistance, Neoplasm: drug effects
/ Proto-Oncogene Proteins c-raf: genetics / Proto-Oncogene
Proteins c-raf: metabolism / Proto-Oncogene Proteins
p21(ras): genetics / Proto-Oncogene Proteins p21(ras):
antagonists $\&$ inhibitors / Proto-Oncogene Proteins
p21(ras): metabolism / Cell Line, Tumor / Mutation / Genes,
Reporter / MAP Kinase Signaling System: drug effects / MAP
Kinase Signaling System: genetics / Apoptosis: drug effects
/ Proto-Oncogene Proteins c-raf (NLM Chemicals) /
Proto-Oncogene Proteins p21(ras) (NLM Chemicals) / KRAS
protein, human (NLM Chemicals) / Raf1 protein, human (NLM
Chemicals)},
cin = {BE01},
ddc = {500},
cid = {I:(DE-He78)BE01-20160331},
pnm = {899 - ohne Topic (POF4-899)},
pid = {G:(DE-HGF)POF4-899},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:40694611},
doi = {10.1126/scisignal.adr3738},
url = {https://inrepo02.dkfz.de/record/303097},
}