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@ARTICLE{Pauli:305504,
author = {C. Pauli$^*$ and M. Kienhöfer$^*$ and M. Blank$^*$ and O.
Begik and C. Rohde and S. Zimmermann$^*$ and L. Werner and
D. Heid and F. Xu$^*$ and K. Weidenauer and S. Delaunay$^*$
and N. K. Krall$^*$ and K. Trunk$^*$ and D. Zhao and F. Zhou
and L. Llovera and O. Alexane and A. Heit-Mondrzyk$^*$ and
U. Platzbecker and C. D. Baldus and H. Serve and M.
Bornhäuser and C. B. Vågbø and S. A. Benitah and J.
Krijgsveld$^*$ and E. M. Novoa and C. Müller-Tidow and M.
Frye$^*$},
title = {{D}isrupting t{RNA} modifications to target mitochondrial
vulnerabilities in drug-resistant leukemia cells.},
journal = {Blood},
volume = {nn},
issn = {0006-4971},
address = {Washington, DC},
publisher = {American Society of Hematology},
reportid = {DKFZ-2025-02191},
pages = {nn},
year = {2025},
note = {#EA:A350#LA:A350# / epub},
abstract = {Dysregulated RNA modifications contribute to cancer
progression and therapy resistance, yet the underlying
mechanism often remains unknown. Here, we perform
CRISPR-based synthetic lethality screens to systematically
explore the role of RNA modifications in mediating
resistance to anti-leukaemic drugs. We identify the
TRMT5-mediated formation of N1-methylguanosine (m1G) in the
tRNA anticodon loop as essential for mediating drug
tolerance to cytarabine and venetoclax in acute myeloid
leukemia (AML). TRMT5 methylates nearly all mitochondrial
and nuclear tRNAs with a guanosine at position 37, but its
role in promoting drug tolerance specifically depends on its
mitochondrial function. TRMT5 is essential for the dynamic
upregulation of mitochondrial mRNA translation and oxidative
phosphorylation (OXPHOS), which are critical for sustaining
drug tolerance in leukemia cells. This mitochondrial
dependency correlates with therapy outcomes in leukemia
patients: lower expression of electron transport chain genes
is linked to poorer outcomes in a cohort of nearly 100 AML
patients undergoing first induction therapy. Finally, we
demonstrate that targeted depletion of TRMT5 protein using a
conditional degron, in conjunction with cytarabine and
venetoclax treatment, synergistically induces cell death in
drug-tolerant AML cells. Thus, our study reveals TRMT5 as
promising drug target for therapy-resistant leukemia.},
cin = {A350 / B230},
ddc = {610},
cid = {I:(DE-He78)A350-20160331 / I:(DE-He78)B230-20160331},
pnm = {311 - Zellbiologie und Tumorbiologie (POF4-311)},
pid = {G:(DE-HGF)POF4-311},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:40749163},
doi = {10.1182/blood.2024027822},
url = {https://inrepo02.dkfz.de/record/305504},
}