% IMPORTANT: The following is UTF-8 encoded. This means that in the presence
% of non-ASCII characters, it will not work with BibTeX 0.99 or older.
% Instead, you should use an up-to-date BibTeX implementation like “bibtex8” or
% “biber”.
@ARTICLE{Fernandez:307431,
author = {N. R. Fernandez and Y. Chang and N. M. Nunes and J. R.
Dimayacyac and A. Levine and A. Ringel and L. Negm and A. B.
Ercan and J. M. Hess and O. Ahmad$^*$ and C. Lee and L.
Stengs and V. Bianchi and M. Edwards and S. Doherty and J.
Chung and L. Nobre and J. Bennett and A. J. Dodgshun and D.
Jones$^*$ and S. Pfister$^*$ and A. Villani and D. Malkin
and V. Ramaswamy and A. Huang and E. Bouffet and M. Aronson
and P. B. Dirks and A. Shlien and G. Getz and Y. E. Maruvka
and B. Ertl-Wagner and C. Hawkins and A. Das and U. Tabori},
title = {{P}atterns of hypermutation shape tumorigenesis and
immunotherapy response in mismatch-repair-deficient glioma.},
journal = {Nature genetics},
volume = {nn},
issn = {1061-4036},
address = {London},
publisher = {Macmillan Publishers Limited, part of Springer Nature},
reportid = {DKFZ-2025-03030},
pages = {nn},
year = {2025},
note = {epub},
abstract = {Primary mismatch-repair-deficient high-grade gliomas
(priMMRD-HGG) are lethal tumors characterized by
hypermutation, resistance to chemoradiation and variable
response to immunotherapy. To investigate the mechanisms
governing the emergence of driver mutations and their impact
on gliomagenesis and patient outcomes, we analyzed genomic
and clinical data from 162 priMMRD-HGG. Here we identified
three subgroups defined by secondary driver mutations in
replicative DNA polymerases or IDH1. These subgroups
converge on glioma drivers through distinct combinations of
genomic instability-generating mechanisms, displaying an
inverse correlation between point mutations and copy number
alterations. MMRD signatures drive the emergence of specific
mutations in TP53 and IDH1, notably excluding common
pediatric glioma drivers. Global hypomethylation stratifies
priMMRD-HGG into a unique methylation cluster.
DNA-polymerasemut priMMRD-HGG exhibit ultrahypermutation, an
immune-hot microenvironment and immunotherapy
responsiveness, whereas IDH1mut priMMRD-HGG are immune-cold
and immunotherapy resistant. MMRD-driven gliomagenesis
defines the role of nonrandom mutagenesis patterns in cancer
development, providing frameworks for targeted and
immune-therapeutics.},
cin = {B360 / B062 / HD01},
ddc = {570},
cid = {I:(DE-He78)B360-20160331 / I:(DE-He78)B062-20160331 /
I:(DE-He78)HD01-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:41430480},
doi = {10.1038/s41588-025-02420-x},
url = {https://inrepo02.dkfz.de/record/307431},
}