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@ARTICLE{Mntyl:307571,
author = {S. Mäntylä and A. Nurminen and S. Huovinen and S.
Jaatinen and T. Haapaniemi and R. Nurminen and I. Hermelo
and S. Volz$^*$ and K. K. Maaß$^*$ and K. W. Pajtler$^*$
and K. Nordfors and H. Haapasalo and M. Nykter and J.
Haapasalo and K. J. Rautajoki},
title = {{G}enomic analysis of {PLNTY}-like tumor progression into
epithelioid glioblastoma: a case report.},
journal = {Acta Neuropathologica Communications},
volume = {nn},
issn = {2051-5960},
address = {London},
publisher = {Biomed Central},
reportid = {DKFZ-2026-00066},
pages = {nn},
year = {2026},
note = {#DKTKZFB26# / epub},
abstract = {Polymorphous low-grade neuroepithelial tumors of the young
(PLNTY) are slow- or non-progressing epileptogenic tumors,
typically occurring in young adults. These tumors are highly
calcified and exhibit both diffuse growth and
oligodendroglioma-like patterns. Epithelioid glioblastomas
(E-GB) are rare and aggressive variants of isocitrate
dehydrogenase wildtype glioblastomas (GB), associated with
poor overall survival. Both PLNTY and E-GB often carry
oncogenic BRAF V600E mutation (BRAFV600E). In this case
study, we analyzed clinical and genetic data from a single
patient who, based on extensive histological and molecular
evaluation, was diagnosed to carry PLNTY-like tumor that
progressed into E-GB years later. The aim of our study was
to uncover the genetic drivers and the evolutionary history
of these tumors. Progression of the PLNTY-like tumor into
E-GB was investigated using histology, chromosomal
karyotyping, whole-genome sequencing (WGS), and RNA
sequencing. A typical immunohistochemical stain pattern of
CD34 positivity was detected in the apparent PLNTY, whereas
it was depleted in the E-GB sample, as expected. WGS
analysis of the PLNTY and three E-GB samples revealed four
genes with shared somatic protein-altering mutations: BRAF
(carrying BRAFV600E), clonal in both PLNTY and E-GB, as well
as GNS, FOXRED2, and SSTR5, which were subclonal in PLNTY
and clonal in E-GB. Both the PLNTY-like and E-GB tumors also
carried highly similar copy number alteration profiles with
a prominent loss of heterozygosity (LOH) in the majority of
the chromosomes, suggesting their monoclonal origin.
PLNTY-like tumor was mainly diploid, and the tumor underwent
a genome-wide duplication event during the progression to
E-GB. Furthermore, two focal rearrangements leading to
homozygous deletion of CDKN2A/B were detected in E-GB
samples. In conclusion, this study revealed unusually
extensive LOH in the histologically and genetically
supported PLNTY-like tumor that progressed into E-GB.
Notably, only a limited set of genetic alterations was
associated with malignant transformation beyond genome
duplication, the CDKN2A/B inactivation representing the
best-known oncogenic driver for malignant transformation.
These findings suggest that genomic profiling may be a
valuable tool for the diagnosis and prognostic assessment of
low-grade neuroepithelial lesions.},
keywords = {Brain tumor (Other) / Cancer (Other) / Cancer genetics
(Other) / Epithelioid glioblastoma (Other) /
Polymorphous-low-grade-neuroepithelial-of-young (Other)},
cin = {B062 / HD01},
ddc = {610},
cid = {I:(DE-He78)B062-20160331 / I:(DE-He78)HD01-20160331},
pnm = {312 - Funktionelle und strukturelle Genomforschung
(POF4-312)},
pid = {G:(DE-HGF)POF4-312},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:41508055},
doi = {10.1186/s40478-025-02209-3},
url = {https://inrepo02.dkfz.de/record/307571},
}