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@ARTICLE{Kppe:310094,
author = {J. Köppe and A. Schiel and C. Gerlinger and H. Götte and
D. Edelmann$^*$ and S. Erdmann},
title = {{I}ntegration of {R}eal-{W}orld {D}ata into {C}linical
{T}rials: {A}n {I}nterdisciplinary {D}iscussion from
{R}egulatory and {P}ractical {P}erspectives. [{E}inbindung
von versorgungsnahen {D}aten in klinische {S}tudien –
{I}nterdisziplinäre {D}iskussion aus regulatorischer und
anwendungsbezogener {S}icht].},
journal = {Das Gesundheitswesen},
volume = {nn},
issn = {0941-3790},
address = {Stuttgart [u.a.]},
publisher = {Thieme},
reportid = {DKFZ-2026-00438},
pages = {nn},
year = {2026},
note = {epub},
abstract = {Increasing efforts are required to integrate the growing
volume of so-called real-world data (also named routine
practice data), which are data generated outside of
randomized controlled trials, into regulatory studies.
Various stakeholders anticipate that such integration could
save time and financial resources during the approval
process of new therapies, and ethical considerations also
partially support such an approach. The aim of this
manuscript is to provide an overview of the methodological,
ethical, and regulatory considerations when integrating
routine practice data into randomized controlled trials. It
targets clinical researchers, biostatisticians, regulators,
and decision-makers involved in evidence generation and
trial design.The inclusion of real-world data in randomized
controlled trials can be meaningful from both ethical and
economic perspectives. However, implementing this requires
addressing various and sometimes significant limitations of
the data, which need to be methodologically addressed.
Therefore, it is essential to carefully weigh the risks and
benefits of incorporating real world data into clinical
studies.Randomized trials remain the gold standard for
evaluating the efficacy of new therapies. Nevertheless,
real-world data have the potential to improve the complex
and costly process of drug development. The assessment of
the potential for a specific clinical study should be made
in collaboration with all relevant stakeholders. Apart from
that, real-world data have a substantial potential to expand
the evidence from randomized trials after post-market
approval, thereby ensuring the safety of all patients.},
subtyp = {Review Article},
cin = {C060},
ddc = {610},
cid = {I:(DE-He78)C060-20160331},
pnm = {313 - Krebsrisikofaktoren und Prävention (POF4-313)},
pid = {G:(DE-HGF)POF4-313},
typ = {PUB:(DE-HGF)16},
pubmed = {pmid:41730277},
doi = {10.1055/a-2736-6561},
url = {https://inrepo02.dkfz.de/record/310094},
}